Annotation Detail

Information
Associated Genes
DMD
Associated Variants
DMD MUTATION
DMD MUTATION
Associated Disease
Becker muscular dystrophy
Source Database
DisGeNET
Description
Exon-skipping therapies aim to convert Duchenne muscular dystrophy (DMD) into less severe Becker muscular dystrophy (BMD) by altering pre-mRNA splicing to restore an open reading frame, allowing translation of an internally deleted and partially functional dystrophin protein.
Pubmed
25612243
Section of the abstract supporting the evidence
OBJECTIVE
Number of the section of the abstract supporting the evidence
1
Number of the sentence supporting the evidence
1
Original source reporting the Gene Disease association
BeFree,CLINVAR,GAD,MGD,ORPHANET,UNIPROT
DisGENET score for the Gene Disease association
0.497741173882984
Drugs