Annotation Detail

Information
Associated Genes
LDLR
Associated Variants
PCSK9 p.Arg46Leu (p.R46L) ( ENST00000302118.5, ENST00000713786.1, ENST00000710286.1 )
PCSK9 p.Arg46Leu (p.R46L) ( ENST00000302118.5, ENST00000710286.1, ENST00000713786.1 )
Associated Disease
Hypercholesterolemia, Familial
Source Database
DisGeNET
Description
1130 unrelated subjects with molecularly defined FH were screened for mutation R46L in the PCSK9 gene and cell culture experiments were performed to study the effect of high concentrations of low density lipoprotein (LDL) on the binding of PCSK9 to the LDL receptor (LDLR).
Pubmed
19917273
Original source reporting the Gene Disease association
BeFree
DisGENET score for the Gene Disease association
0.462660055576745
Year of publication
2010
Drugs