Annotation Detail

Information
Associated Genes
ABCA4 LOC126805793
Associated Variants
ABCA4 p.Ile1562Thr (p.I1562T) ( ENST00000370225.4 )
ABCA4 p.Ile1562Thr (p.I1562T) ( ENST00000370225.4 )
Associated Disease
Stargardt disease Severe early-childhood-onset retinal dystrophy
Source Database
ClinVar
Description
NM_000350.3(ABCA4):c.4685T>C (p.Ile1562Thr) AND multiple conditions
ClinVar Allele ID
105200
ClinVar RefSeq Alternation Syntax
NM_001425324.1:c.4463T>C
ClinVar RefSeq Alternation Syntax
NM_000350.3:c.4685T>C
Clinical Significance Description
Likely pathogenic
Clinical Significance Last Update
2023-01-11
Clinical Significance Review Status
criteria provided, single submitter
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV002509209
ClinVar Disease
Severe early-childhood-onset retinal dystrophy
ClinVar Disease
Stargardt disease
Observed Origin Sample
germline
Drugs