Inherited bone marrow failure syndrome
Information
- Disease name
- Inherited bone marrow failure syndrome
- Disease ID
- Description
Disease area statistics
[No Data.]
Chromosome band
[No Data.]
Annotation
| Genes | Mutation | Description | Source | Links |
|---|
| NCT ID | Status | Phase | Summary | Start date | Completion date |
|---|---|---|---|---|---|
| NCT02958462 | Recruiting | N/A | Pre-myeloid Cancer and Bone Marrow Failure Clinic Study | January 16, 2017 | September 15, 2035 |
| NCT05687149 | Recruiting | Defining the Natural History of Squamous Cell Carcinoma in Fanconi Anemia | March 23, 2023 | December 31, 2035 | |
| NCT05796570 | Recruiting | Phase 2 | A Pilot Study to Evaluate the Feasibility of Post-Hematopoietic Stem Cell Transplant Prophylaxis With Decitabine Combined With Filgrastim for Children and Young Adults With AML, MDS and Related Myeloid Malignancies | April 19, 2023 | September 1, 2029 |
| NCT06090669 | Recruiting | Phase 1 | Imatinib to Increase RUNX1 Activity in Participants With Germline RUNX1 Deficiency | December 19, 2023 | October 30, 2027 |
| NCT02231710 | Terminated | Phase 1 | Safety Study of Gene Modified Donor T Cell Infusion After Stem Cell Transplant for Non-Malignant Diseases | February 2015 | January 2018 |