Bone Marrow failure syndromes
Information
- Disease name
- Bone Marrow failure syndromes
- Disease ID
- Description
Disease area statistics
[No Data.]
Chromosome band
[No Data.]
Annotation
| Genes | Mutation | Description | Source | Links |
|---|
| NCT ID | Status | Phase | Summary | Start date | Completion date |
|---|---|---|---|---|---|
| NCT02722668 | Active, not recruiting | Phase 2 | UCB Transplant for Hematological Diseases Using a Non Myeloablative Prep | May 15, 2017 | December 2029 |
| NCT00774527 | Completed | Phase 3 | Comparison of Cy-Atg Vs Cy-Flu-Atg for the Conditioning Therapy in Allo-HCT | March 2003 | January 2011 |
| NCT02337595 | Completed | Phase 1/Phase 2 | Memory T-cell Infusion to Improve Immunity After TCR-alpha/Beta Depleted Hematopoietic Stem Cell Transplantation | August 2014 | January 2016 |
| NCT02055456 | Completed | Phase 1/Phase 2 | Nandrolone Decanoate in the Treatment of Telomeropathies | February 1, 2014 | February 1, 2017 |
| NCT02224872 | Completed | Phase 2 | Transplantation of Partially Mismatched Related or Matched Unrelated Bone Marrow for Patients With Refractory Severe Aplastic Anemia | August 2014 | December 2021 |
| NCT02277639 | Completed | Phase 2 | Reduced Intensity Conditioning Using CD3+/CD19+ Depletion for Non Malignant Transplantable Diseases | November 2011 | March 2016 |
| NCT02349906 | Completed | Phase 2 | Treosulfan-based Versus Busulfan-based Conditioning in Paediatric Patients With Non-malignant Diseases | April 2015 | April 2023 |
| NCT03128996 | Recruiting | Phase 1/Phase 2 | Reduced Intensity Conditioning and Familial HLA-Mismatched BMT for Non-Malignant Disorders | March 20, 2017 | April 2026 |
| NCT02356653 | Recruiting | Early Phase 1 | Expanded Access Protocol Using CD3+/CD19+ Depleted PBSC | December 2013 | January 2027 |
| NCT02720679 | Recruiting | Investigation of the Genetics of Hematologic Diseases | June 17, 2016 | July 2050 | |
| NCT02928991 | Recruiting | Early Phase 1 | Fludarabine Based RIC for Bone Marrow Failure Syndromes | April 2015 | December 2026 |
| NCT01050439 | Terminated | Phase 2 | Unrelated Donor Transplant for Malignant and Non-Malignant Disorders | November 2002 | April 2011 |
| NCT00315419 | Unknown status | Identifying Characteristics of Bone Marrow Failure Syndromes | April 2006 | July 2009 | |
| NCT01419704 | Withdrawn | Phase 1/Phase 2 | Phase I/II Pilot Study of Mixed Chimerism to Treat Hemoglobinopathies | May 2011 | May 2016 |