Amyloid Neuropathies, Familial
Information
- Disease name
- Amyloid Neuropathies, Familial
- Disease ID
- Description
Disease area statistics
[No Data.]
Chromosome band
[No Data.]
Annotation
| Genes | Mutation | Description | Source | Links |
|---|
| NCT ID | Status | Phase | Summary | Start date | Completion date |
|---|---|---|---|---|---|
| NCT03431896 | Active, not recruiting | Monitoring of Early Disease Progression in Hereditary Transthyretin Amyloidosis | February 1, 2018 | December 31, 2026 | |
| NCT02939820 | Approved for marketing | Expanded Access Protocol of Patisiran for Patients With Hereditary ATTR Amyloidosis (hATTR) | |||
| NCT01960348 | Completed | Phase 3 | APOLLO: The Study of an Investigational Drug, Patisiran (ALN-TTR02), for the Treatment of Transthyretin (TTR)-Mediated Amyloidosis | November 2013 | August 2017 |
| NCT02319005 | Completed | Phase 3 | ENDEAVOUR: Phase 3 Multicenter Study of Revusiran (ALN-TTRSC) in Patients With Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC) | December 2014 | March 30, 2017 |
| NCT03720275 | Completed | N/A | Early and Systematic Screening in Chronic Neuropathy | November 27, 2018 | December 23, 2021 |
- MeSH unique ID (MeSH (Medical Subject Headings))
- D028227