Thalassemia Intermedia

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Information
Disease name
Thalassemia Intermedia
Disease ID
Description
Disease area statistics
[No Data.]
Chromosome band
[No Data.]
Annotation
Genes Mutation Description Source Links
NCT ID Status Phase Summary Start date Completion date
NCT01140321 Completed Phase 2 Efficacy and Safety of Neridronate (Nerixia®)to Treat Osteoporosis in Patients With TM and TI January 2004 May 2010
NCT01224496 Completed Phase 1/Phase 2 Traditional Chinese Medicine in the Supportive Management of Anaemic and Cytopenic (Leukopenia, Thrombocytopenia) Haematological Disorders July 2009 August 2011
NCT01496963 Completed Prevalence of Pulmonary Hypertension (PAH) in Patients With Thalassemia January 2012 December 2021
NCT05444894 Recruiting Phase 1/Phase 2 EDIT-301 for Autologous Hematopoietic Stem Cell Transplant (HSCT) in Participants With Transfusion-Dependent Beta Thalassemia (TDT) April 29, 2022 December 2025
NCT06137079 Recruiting "Iron Overload and Endocrinological Diseases" June 20, 2013 December 31, 2025
NCT01624038 Unknown status Phase 2/Phase 3 Therapeutic Effect and Safety of Combined Hydroxyurea With Recombinant Human Erythropoietin. June 2012 December 2012