Amyloidosis, Familial

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Information
Disease name
Amyloidosis, Familial
Disease ID
Description
Disease area statistics
[No Data.]
Chromosome band
[No Data.]
Annotation
Genes Mutation Description Source Links
NCT ID Status Phase Summary Start date Completion date
NCT03862807 Completed Phase 3 Patisiran in Patients With Hereditary Transthyretin-mediated Amyloidosis (hATTR Amyloidosis) Disease Progression Post-Liver Transplant March 27, 2019 October 20, 2020
NCT05489549 Recruiting Subclinical Transthyretin Cardiac Amyloidosis in V122I TTR Carriers November 21, 2022 June 30, 2027
MeSH unique ID (MeSH (Medical Subject Headings))
D028226