Infantile malignant osteopetrosis

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Information
Disease name
Infantile malignant osteopetrosis
Disease ID
Description
Disease area statistics
[No Data.]
Chromosome band
[No Data.]
Annotation
Genes Mutation Description Source Links
NCT ID Status Phase Summary Start date Completion date
NCT04525352 Terminated Phase 1 A Trial to Evaluate Safety and Efficacy of RP-L401-0120 in Subjects With Infantile Malignant Osteopetrosis November 19, 2020 May 21, 2021