Infantile malignant osteopetrosis
Information
- Disease name
- Infantile malignant osteopetrosis
- Disease ID
- Description
Disease area statistics
[No Data.]
Chromosome band
[No Data.]
Annotation
Genes | Mutation | Description | Source | Links |
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NCT ID | Status | Phase | Summary | Start date | Completion date |
---|---|---|---|---|---|
NCT04525352 | Terminated | Phase 1 | A Trial to Evaluate Safety and Efficacy of RP-L401-0120 in Subjects With Infantile Malignant Osteopetrosis | November 19, 2020 | May 21, 2021 |