Annotation Detail

Information
Associated Genes
PAH
Associated Variants
PAH p.Ala395Pro (p.A395P) ( ENST00000553106.6, ENST00000307000.7 )
PAH p.Arg261Pro (p.R261P) ( ENST00000307000.7, ENST00000553106.6 )
PAH p.Arg261Gln (p.R261Q) ( ENST00000553106.6, ENST00000307000.7 )
PAH p.Ala395Pro (p.A395P) ( ENST00000307000.7, ENST00000553106.6 )
PAH p.Arg261Pro (p.R261P) ( ENST00000307000.7, ENST00000553106.6 )
PAH p.Arg261Gln (p.R261Q) ( ENST00000307000.7, ENST00000553106.6 )
Associated Disease
Phenylketonurias
Source Database
DisGeNET
Description
We report two new patients with tetrahydrobiopterin (BH4)-responsive phenylketonuria and compare their phenylalanine hydroxylase (PAH) genotypes (A395P/ IVS12+g>a and R261Q/165T, respectively) to those of previous cases from the literature.
Pubmed
11999982
Original source reporting the Gene Disease association
BeFree
DisGENET score for the Gene Disease association
0.374728566641762
Year of publication
2002
Drugs