Annotation Detail

Information
Associated Genes
GAA
Associated Variants
GAA p.Ser251Leu (p.S251L) ( ENST00000577106.6, ENST00000570803.6, ENST00000390015.7, ENST00000302262.8, ENST00000714054.1, ENST00000714055.1, ENST00000714057.1, ENST00000714058.1, ENST00000714062.1 )
GAA p.Ser254Leu (p.S254L) ( ENST00000570803.6, ENST00000577106.6, ENST00000302262.8, ENST00000390015.7, ENST00000714054.1, ENST00000714055.1, ENST00000714057.1, ENST00000714058.1, ENST00000714062.1 )
GAA p.Glu262Lys (p.E262K) ( ENST00000390015.7, ENST00000570803.6, ENST00000714062.1, ENST00000714057.1, ENST00000714054.1, ENST00000577106.6, ENST00000714058.1, ENST00000302262.8, ENST00000714055.1 )
GAA p.Gly615Arg (p.G615R) ( ENST00000714057.1, ENST00000577106.6, ENST00000714054.1, ENST00000570803.6, ENST00000390015.7, ENST00000714062.1, ENST00000302262.8, ENST00000714055.1, ENST00000714058.1 )
GAA p.Asp645Glu (p.D645E) ( ENST00000714055.1, ENST00000302262.8, ENST00000714058.1, ENST00000714062.1, ENST00000390015.7, ENST00000570803.6, ENST00000577106.6, ENST00000714054.1, ENST00000714057.1 )
GAA p.Asp645= (p.D645=) ( ENST00000714057.1, ENST00000714054.1, ENST00000577106.6, ENST00000390015.7, ENST00000570803.6, ENST00000714062.1, ENST00000714058.1, ENST00000714055.1, ENST00000302262.8 )
GAA p.Ser251Leu (p.S251L) ( ENST00000302262.8, ENST00000390015.7, ENST00000570803.6, ENST00000577106.6, ENST00000714054.1, ENST00000714055.1, ENST00000714057.1, ENST00000714058.1, ENST00000714062.1 )
GAA p.Ser254Leu (p.S254L) ( ENST00000302262.8, ENST00000390015.7, ENST00000570803.6, ENST00000577106.6, ENST00000714054.1, ENST00000714055.1, ENST00000714057.1, ENST00000714058.1, ENST00000714062.1 )
GAA p.Glu262Lys (p.E262K) ( ENST00000302262.8, ENST00000390015.7, ENST00000570803.6, ENST00000577106.6, ENST00000714054.1, ENST00000714055.1, ENST00000714057.1, ENST00000714058.1, ENST00000714062.1 )
GAA p.Gly615Arg (p.G615R) ( ENST00000302262.8, ENST00000390015.7, ENST00000570803.6, ENST00000577106.6, ENST00000714054.1, ENST00000714055.1, ENST00000714057.1, ENST00000714058.1, ENST00000714062.1 )
GAA p.Asp645Glu (p.D645E) ( ENST00000302262.8, ENST00000390015.7, ENST00000570803.6, ENST00000577106.6, ENST00000714054.1, ENST00000714055.1, ENST00000714057.1, ENST00000714058.1, ENST00000714062.1 )
GAA p.Asp645= (p.D645=) ( ENST00000302262.8, ENST00000390015.7, ENST00000570803.6, ENST00000577106.6, ENST00000714054.1, ENST00000714055.1, ENST00000714057.1, ENST00000714058.1, ENST00000714062.1 )
Associated Disease
Glycogen storage disease type II
Source Database
DisGeNET
Description
Therefore, newborn screening for Pompe disease could be successfully conducted by including genotyping and lymphocyte GAA assay, even in a population with mutation heterozygosity and pseudodeficiency.
Pubmed
20080426
Original source reporting the Gene Disease association
UNIPROT
DisGENET score for the Gene Disease association
0.499337113635194
Year of publication
2010
Drugs