Annotation Detail

Information
Associated Genes
GAA
Associated Variants
GAA MUTATION
GAA MUTATION
Associated Disease
Glycogen storage disease type II
Source Database
DisGeNET
Description
Pompe disease is a rare multi-systemic metabolic myopathy caused by autosomal recessive mutations in the acidic alpha glucosidase (GAA) gene.
Pubmed
25037089
Section of the abstract supporting the evidence
ALL_TEXT_1/3
Number of the section of the abstract supporting the evidence
1
Number of the sentence supporting the evidence
1
Original source reporting the Gene Disease association
BeFree,CLINVAR,CTD_human,GAD,LHGDN,MGD,UNIPROT
DisGENET score for the Gene Disease association
0.499337113635194
Drugs