Annotation Detail

Information
Associated Genes
GAA
Associated Variants
GAA p.Lys849ArgfsTer38 (p.K849Rfs*38) ( ENST00000302262.8, ENST00000714055.1, ENST00000714058.1, ENST00000714057.1, ENST00000577106.6, ENST00000714054.1, ENST00000390015.7, ENST00000570803.6, ENST00000714062.1 )
GAA p.Lys849ArgfsTer38 (p.K849Rfs*38) ( ENST00000302262.8, ENST00000390015.7, ENST00000570803.6, ENST00000577106.6, ENST00000714054.1, ENST00000714055.1, ENST00000714057.1, ENST00000714058.1, ENST00000714062.1 )
Associated Disease
glycogen storage disease
Source Database
ClinVar
Description
NM_000152.5(GAA):c.2544del (p.Lys849fs) AND Glycogen storage disease
ClinVar Allele ID
98389
ClinVar RefSeq Alternation Syntax
NM_001079804.3:c.2544del
ClinVar RefSeq Alternation Syntax
NM_001079803.3:c.2544del
ClinVar RefSeq Alternation Syntax
NM_000152.5:c.2544del
Clinical Significance Description
Pathogenic
Clinical Significance Last Update
2015-12-23
Clinical Significance Review Status
criteria provided, single submitter
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV004017389
ClinVar Disease
Glycogen storage disease
Observed Origin Sample
germline
Drugs