Annotation Detail

Information
Associated Genes
ABCA4
Associated Variants
ABCA4 p.Gly991Arg (p.G991R) ( ENST00000370225.4 )
ABCA4 p.Gly991Arg (p.G991R) ( ENST00000370225.4 )
Associated Disease
Severe early-childhood-onset retinal dystrophy
Source Database
ClinVar
Description
NM_000350.3(ABCA4):c.2971G>C (p.Gly991Arg) AND Severe early-childhood-onset retinal dystrophy
ClinVar Allele ID
105071
ClinVar RefSeq Alternation Syntax
NM_000350.3:c.2971G>C
ClinVar RefSeq Alternation Syntax
NM_001425324.1:c.2749G>C
Clinical Significance Description
Likely pathogenic
Clinical Significance Last Update
2024-03-29
Clinical Significance Review Status
criteria provided, single submitter
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV003989317
ClinVar Disease
Severe early-childhood-onset retinal dystrophy
Observed Origin Sample
germline
Drugs