Annotation Detail

Information
Associated Genes
GNPTAB
Associated Variants
GNPTAB p.Ser15Tyr (p.S15Y) ( ENST00000549165.1, ENST00000392919.4, ENST00000549940.5, ENST00000299314.12 )
GNPTAB p.Ser15Tyr (p.S15Y) ( ENST00000299314.12, ENST00000392919.4, ENST00000549165.1, ENST00000549940.5 )
Associated Disease
Pseudo-Hurler polydystrophy Mucolipidosis type II
Source Database
ClinVar
Description
NM_024312.5(GNPTAB):c.44C>A (p.Ser15Tyr) AND multiple conditions
ClinVar Allele ID
47684
ClinVar RefSeq Alternation Syntax
NM_024312.5:c.44C>A
Clinical Significance Description
Likely pathogenic
Clinical Significance Last Update
2023-09-08
Clinical Significance Review Status
criteria provided, single submitter
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV003764648
ClinVar Disease
Pseudo-Hurler polydystrophy
ClinVar Disease
Mucolipidosis type II
Observed Origin Sample
germline
Drugs