Annotation Detail

Information
Associated Genes
GNPTAB
Associated Variants
GNPTAB p.Ile656Ter (p.I656*) ( ENST00000299314.12 )
GNPTAB p.Ile656Ter (p.I656*) ( ENST00000299314.12 )
Associated Disease
Mucolipidosis type II Pseudo-Hurler polydystrophy
Source Database
ClinVar
Description
NM_024312.5(GNPTAB):c.1965del (p.Pro655_Ile656insTer) AND multiple conditions
ClinVar Allele ID
47645
ClinVar RefSeq Alternation Syntax
NM_024312.5:c.1965del
Clinical Significance Description
Pathogenic
Clinical Significance Last Update
2023-03-21
Clinical Significance Review Status
criteria provided, single submitter
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV003764647
ClinVar Disease
Pseudo-Hurler polydystrophy
ClinVar Disease
Mucolipidosis type II
Observed Origin Sample
germline
Drugs