Annotation Detail

Information
Associated Genes
IDUA
Associated Variants
IDUA p.Tyr625Cys (p.Y625C) ( ENST00000247933.9, ENST00000514224.2 )
IDUA p.Tyr625Cys (p.Y625C) ( ENST00000247933.9, ENST00000514224.2 )
Associated Disease
Mucopolysaccharidosis type 1
Source Database
ClinVar
Description
NM_000203.5(IDUA):c.1874A>G (p.Tyr625Cys) AND Mucopolysaccharidosis type 1
ClinVar Allele ID
106588
ClinVar RefSeq Alternation Syntax
NM_001363576.1:c.1478A>G
ClinVar RefSeq Alternation Syntax
NM_000203.5:c.1874A>G
ClinVar RefSeq Alternation Syntax
NR_110313.1:n.1966A>G
Clinical Significance Description
Likely pathogenic
Clinical Significance Last Update
2022-04-14
Clinical Significance Review Status
criteria provided, single submitter
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV002515779
ClinVar Disease
Mucopolysaccharidosis type 1
Observed Origin Sample
germline
Drugs