Annotation Detail

Information
Associated Genes
GNPTAB
Associated Variants
GNPTAB p.Trp81Leu (p.W81L) ( ENST00000299314.12, ENST00000549940.5 )
GNPTAB p.Trp81Leu (p.W81L) ( ENST00000299314.12, ENST00000549940.5 )
Associated Disease
Pseudo-Hurler polydystrophy Mucolipidosis type II
Source Database
ClinVar
Description
NM_024312.5(GNPTAB):c.242G>T (p.Trp81Leu) AND multiple conditions
ClinVar Allele ID
47656
ClinVar RefSeq Alternation Syntax
NM_024312.5:c.242G>T
Clinical Significance Description
Likely pathogenic
Clinical Significance Last Update
2022-09-28
Clinical Significance Review Status
criteria provided, single submitter
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV002514130
ClinVar Disease
Pseudo-Hurler polydystrophy
ClinVar Disease
Mucolipidosis type II
Observed Origin Sample
germline
Drugs