Annotation Detail

Information
Associated Genes
GNPTAB
Associated Variants
GNPTAB p.Arg1031Ter (p.R1031*) ( ENST00000299314.12 )
GNPTAB p.Arg1031Ter (p.R1031*) ( ENST00000299314.12 )
Associated Disease
Pseudo-Hurler polydystrophy
Source Database
ClinVar
Description
NM_024312.5(GNPTAB):c.3091C>T (p.Arg1031Ter) AND Pseudo-Hurler polydystrophy
ClinVar Allele ID
47668
ClinVar RefSeq Alternation Syntax
NM_024312.5:c.3091C>T
Clinical Significance Description
Pathogenic
Clinical Significance Last Update
2021-09-02
Clinical Significance Review Status
criteria provided, single submitter
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV002288528
ClinVar Disease
Pseudo-Hurler polydystrophy
Observed Origin Sample
germline
Drugs