Annotation Detail

Information
Associated Genes
GNPTAB
Associated Variants
GNPTAB p.Asp1018Gly (p.D1018G) ( ENST00000299314.12 )
GNPTAB p.Asp1018Gly (p.D1018G) ( ENST00000299314.12 )
Associated Disease
Mucolipidosis type II Pseudo-Hurler polydystrophy
Source Database
ClinVar
Description
NM_024312.5(GNPTAB):c.3053A>G (p.Asp1018Gly) AND multiple conditions
ClinVar Allele ID
49680
ClinVar RefSeq Alternation Syntax
NM_024312.5:c.3053A>G
Clinical Significance Description
Likely pathogenic
Clinical Significance Last Update
2023-11-07
Clinical Significance Review Status
criteria provided, single submitter
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV001852693
ClinVar Disease
Pseudo-Hurler polydystrophy
ClinVar Disease
Mucolipidosis type II
Observed Origin Sample
germline
Drugs