Annotation Detail

Information
Associated Genes
SMPD1
Associated Variants
SMPD1 p.Ala484Glu (p.A484E) ( ENST00000342245.9, ENST00000527275.5 )
SMPD1 p.Ala484Glu (p.A484E) ( ENST00000342245.9, ENST00000527275.5 )
Associated Disease
Niemann-Pick disease, type A Niemann-Pick disease, type B
Source Database
ClinVar
Description
NM_000543.5(SMPD1):c.1451C>A (p.Ala484Glu) AND multiple conditions
ClinVar Allele ID
18034
ClinVar RefSeq Alternation Syntax
NM_000543.5:c.1451C>A
ClinVar RefSeq Alternation Syntax
NM_001007593.3:c.1448C>A
ClinVar RefSeq Alternation Syntax
NR_134502.2:n.923C>A
ClinVar RefSeq Alternation Syntax
NM_001318087.2:c.1451C>A
ClinVar RefSeq Alternation Syntax
NM_001365135.2:c.1319C>A
ClinVar RefSeq Alternation Syntax
NM_001318088.2:c.530C>A
ClinVar RefSeq Alternation Syntax
NR_027400.3:n.1404C>A
Clinical Significance Description
Pathogenic
Clinical Significance Last Update
2023-03-07
Clinical Significance Review Status
criteria provided, single submitter
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV001851602
ClinVar Disease
Niemann-Pick disease, type A
ClinVar Disease
Niemann-Pick disease, type B
Observed Origin Sample
germline
Drugs