Annotation Detail

Information
Associated Genes
GNPTAB
Associated Variants
GNPTAB p.Lys244AsnfsTer10 (p.K244Nfs*10) ( ENST00000549940.5, ENST00000299314.12 )
GNPTAB p.Lys244AsnfsTer10 (p.K244Nfs*10) ( ENST00000299314.12, ENST00000549940.5 )
Associated Disease
Pseudo-Hurler polydystrophy Mucolipidosis type II
Source Database
ClinVar
Description
NM_024312.5(GNPTAB):c.732_733del (p.Lys244fs) AND multiple conditions
ClinVar Allele ID
102018
ClinVar RefSeq Alternation Syntax
NM_024312.5:c.732_733del
Clinical Significance Description
Pathogenic
Clinical Significance Last Update
2023-01-14
Clinical Significance Review Status
criteria provided, single submitter
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV001388068
ClinVar Disease
Pseudo-Hurler polydystrophy
ClinVar Disease
Mucolipidosis type II
Observed Origin Sample
germline
Drugs