Annotation Detail

Information
Associated Genes
GNPTAB
Associated Variants
GNPTAB p.Gln104Ter (p.Q104*) ( ENST00000549940.5, ENST00000299314.12 )
GNPTAB p.Gln104Ter (p.Q104*) ( ENST00000299314.12, ENST00000549940.5 )
Associated Disease
Mucolipidosis type II Pseudo-Hurler polydystrophy
Source Database
ClinVar
Description
NM_024312.5(GNPTAB):c.310C>T (p.Gln104Ter) AND multiple conditions
ClinVar Allele ID
17802
ClinVar RefSeq Alternation Syntax
NM_024312.5:c.310C>T
Clinical Significance Description
Pathogenic
Clinical Significance Last Update
2023-11-17
Clinical Significance Review Status
criteria provided, single submitter
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV001380992
ClinVar Disease
Pseudo-Hurler polydystrophy
ClinVar Disease
Mucolipidosis type II
Observed Origin Sample
germline
Drugs