Annotation Detail

Information
Associated Genes
ABCA4
Associated Variants
ABCA4 p.Asn1868Ile (p.N1868I) ( ENST00000370225.4 )
ABCA4 p.Arg537His (p.R537H) ( ENST00000370225.4, ENST00000649773.1 )
ABCA4 p.Asn1868Ile (p.N1868I) ( ENST00000370225.4 )
ABCA4 p.Arg537His (p.R537H) ( ENST00000370225.4, ENST00000649773.1 )
Associated Disease
Severe early-childhood-onset retinal dystrophy
Source Database
ClinVar
Description
NM_000350.3(ABCA4):c.[1610G>A;5603A>T] AND Severe early-childhood-onset retinal dystrophy
ClinVar Allele ID
105279
ClinVar Allele ID
104954
ClinVar RefSeq Alternation Syntax
NM_001425324.1:c.1610G>A
ClinVar RefSeq Alternation Syntax
NM_001425324.1:c.5381A>T
ClinVar RefSeq Alternation Syntax
NM_000350.3:c.1610G>A
ClinVar RefSeq Alternation Syntax
NM_000350.3:c.5603A>T
Clinical Significance Description
Likely pathogenic
Clinical Significance Last Update
2021-01-30
Clinical Significance Review Status
criteria provided, single submitter
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV001353019
ClinVar Disease
Severe early-childhood-onset retinal dystrophy
Observed Origin Sample
germline
Drugs