Annotation Detail

Information
Associated Genes
GNPTAB
Associated Variants
GNPTAB p.Ala994SerfsTer8 (p.A994Sfs*8) ( ENST00000299314.12 )
GNPTAB p.Ala994SerfsTer8 (p.A994Sfs*8) ( ENST00000299314.12 )
GNPTAB c.2715+1G>A ( ENST00000299314.12 )
GNPTAB c.2715+1G>A ( ENST00000299314.12 )
Associated Disease
Pseudo-Hurler polydystrophy
Source Database
ClinVar
Description
NM_024312.5(GNPTAB):c.[2715+1G>A;2980_2983del] AND Pseudo-Hurler polydystrophy
ClinVar Allele ID
985746
ClinVar Allele ID
17807
ClinVar RefSeq Alternation Syntax
NM_024312.5:c.2980_2983del
ClinVar RefSeq Alternation Syntax
NM_024312.5:c.2715+1G>A
Clinical Significance Description
Pathogenic
Clinical Significance Last Update
2019-05-31
Clinical Significance Review Status
no assertion criteria provided
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV001293695
ClinVar Disease
Pseudo-Hurler polydystrophy
Observed Origin Sample
inherited
Drugs