Annotation Detail

Information
Associated Genes
SMPD1
Associated Variants
SMPD1 p.Leu304Pro (p.L304P) ( ENST00000527275.5, ENST00000342245.9 )
SMPD1 p.Leu304Pro (p.L304P) ( ENST00000342245.9, ENST00000527275.5 )
Associated Disease
Niemann-Pick disease, type B
Source Database
ClinVar
Description
NM_000543.5(SMPD1):c.911T>C (p.Leu304Pro) AND Niemann-Pick disease, type B
ClinVar Allele ID
18028
Clinical Significance Description
Pathogenic
Clinical Significance Last Update
2015-09-10
Clinical Significance Review Status
no assertion criteria provided
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV000984009
ClinVar Disease
Niemann-Pick disease, type B
Observed Origin Sample
unknown
Drugs