Annotation Detail

Information
Associated Genes
GNPTAB
Associated Variants
GNPTAB p.Leu1137Ter (p.L1137*) ( ENST00000299314.12 )
GNPTAB p.Leu1137Ter (p.L1137*) ( ENST00000299314.12 )
Associated Disease
Pseudo-Hurler polydystrophy
Source Database
ClinVar
Description
NM_024312.5(GNPTAB):c.3410T>A (p.Leu1137Ter) AND Pseudo-Hurler polydystrophy
ClinVar Allele ID
47674
ClinVar RefSeq Alternation Syntax
NM_024312.5:c.3410T>A
Clinical Significance Description
Likely pathogenic
Clinical Significance Last Update
2018-01-10
Clinical Significance Review Status
no assertion criteria provided
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV000983987
ClinVar Disease
Pseudo-Hurler polydystrophy
Observed Origin Sample
unknown
Drugs