Annotation Detail

Information
Associated Genes
GNPTAB
Associated Variants
GNPTAB p.Arg375Ter (p.R375*) ( ENST00000549940.5, ENST00000299314.12 )
GNPTAB p.Arg375Ter (p.R375*) ( ENST00000299314.12, ENST00000549940.5 )
Associated Disease
Pseudo-Hurler polydystrophy
Source Database
ClinVar
Description
NM_024312.5(GNPTAB):c.1123C>T (p.Arg375Ter) AND Pseudo-Hurler polydystrophy
ClinVar Allele ID
47625
ClinVar RefSeq Alternation Syntax
NM_024312.5:c.1123C>T
Clinical Significance Description
Pathogenic
Clinical Significance Last Update
2017-09-28
Clinical Significance Review Status
no assertion criteria provided
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV000983986
ClinVar Disease
Pseudo-Hurler polydystrophy
Observed Origin Sample
unknown
Drugs