Annotation Detail

Information
Associated Genes
ATP1A3
Associated Variants
ATP1A3 p.Arg769Cys (p.R769C), ENSG00000285505 p.Arg756Cys (p.R756C) ( ENST00000545399.6, ENST00000602133.5, ENST00000543770.5, ENST00000648268.1 )
ATP1A3 p.Arg769Cys (p.R769C), ENSG00000285505 p.Arg756Cys (p.R756C) ( ENST00000543770.5, ENST00000545399.6, ENST00000602133.5, ENST00000648268.1 )
Associated Disease
Alternating hemiplegia of childhood 2 dystonia 12 Cerebellar ataxia-areflexia-pes cavus-optic atrophy-sensorineural hearing loss syndrome
Source Database
ClinVar
Description
NM_152296.5(ATP1A3):c.2266C>T (p.Arg756Cys) AND multiple conditions
ClinVar Allele ID
413523
ClinVar RefSeq Alternation Syntax
NM_001256214.2:c.2305C>T
ClinVar RefSeq Alternation Syntax
NM_152296.5:c.2266C>T
ClinVar RefSeq Alternation Syntax
NM_001256213.2:c.2299C>T
Clinical Significance Description
Likely pathogenic
Clinical Significance Last Update
2018-10-12
Clinical Significance Review Status
criteria provided, single submitter
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV000850500
ClinVar Disease
Cerebellar ataxia-areflexia-pes cavus-optic atrophy-sensorineural hearing loss syndrome
ClinVar Disease
Dystonia 12
ClinVar Disease
Alternating hemiplegia of childhood 2
Observed Origin Sample
germline
Drugs