Annotation Detail

Information
Associated Genes
GNPTAB
Associated Variants
GNPTAB p.Ser685LysfsTer61 (p.S685Kfs*61) ( ENST00000299314.12 )
GNPTAB p.Ser685LysfsTer61 (p.S685Kfs*61) ( ENST00000299314.12 )
Associated Disease
Pseudo-Hurler polydystrophy Mucolipidosis type II
Source Database
ClinVar
Description
NM_024312.5(GNPTAB):c.2053_2057del (p.Ser685fs) AND multiple conditions
ClinVar Allele ID
46976
ClinVar RefSeq Alternation Syntax
NM_024312.5:c.2053_2057del
Clinical Significance Description
Pathogenic/Likely pathogenic
Clinical Significance Last Update
2023-01-16
Clinical Significance Review Status
criteria provided, multiple submitters, no conflicts
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV000674766
ClinVar Disease
Pseudo-Hurler polydystrophy
ClinVar Disease
Mucolipidosis type II
Observed Origin Sample
germline
Observed Origin Sample
unknown
Drugs