Annotation Detail

Information
Associated Genes
GNPTAB
Associated Variants
GNPTAB p.Asn759Ter (p.N759*) ( ENST00000299314.12 )
GNPTAB p.Asn759Ter (p.N759*) ( ENST00000299314.12 )
Associated Disease
Pseudo-Hurler polydystrophy Mucolipidosis type II
Source Database
ClinVar
Description
NM_024312.5(GNPTAB):c.2275_2276del (p.Thr758_Asn759insTer) AND multiple conditions
ClinVar Allele ID
47652
ClinVar RefSeq Alternation Syntax
NM_024312.5:c.2275_2276del
Clinical Significance Description
Likely pathogenic
Clinical Significance Last Update
2017-12-05
Clinical Significance Review Status
criteria provided, single submitter
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV000671256
ClinVar Disease
Pseudo-Hurler polydystrophy
ClinVar Disease
Mucolipidosis type II
Observed Origin Sample
unknown
Drugs