Annotation Detail

Information
Associated Genes
ABCA4
Associated Variants
ABCA4 p.Arg2030Gln (p.R2030Q) ( ENST00000370225.4 )
ABCA4 p.? (p.?) ( ENST00000649773.1, ENST00000370225.4 )
ABCA4 p.Arg2030Gln (p.R2030Q) ( ENST00000370225.4 )
ABCA4 p.? (p.?) ( ENST00000370225.4, ENST00000649773.1 )
Associated Disease
Severe early-childhood-onset retinal dystrophy
Source Database
ClinVar
Description
NM_000350.2(ABCA4):c.[1A>G;6089G>A] AND Severe early-childhood-onset retinal dystrophy
ClinVar Allele ID
105317
ClinVar Allele ID
104999
ClinVar RefSeq Alternation Syntax
NM_001425324.1:c.1A>G
ClinVar RefSeq Alternation Syntax
NM_000350.3:c.1A>G
ClinVar RefSeq Alternation Syntax
NM_000350.3:c.6089G>A
ClinVar RefSeq Alternation Syntax
NM_001425324.1:c.5867G>A
Clinical Significance Description
Pathogenic
Clinical Significance Last Update
2016-01-01
Clinical Significance Review Status
criteria provided, single submitter
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV000408532
ClinVar Disease
Severe early-childhood-onset retinal dystrophy
Observed Origin Sample
germline
Drugs