Annotation Detail

Information
Associated Genes
GAA
Associated Variants
GAA c.2646+2T>A ( ENST00000302262.8, ENST00000714055.1, ENST00000714058.1, ENST00000390015.7, ENST00000570803.6, ENST00000714062.1, ENST00000714057.1, ENST00000577106.6, ENST00000714054.1 )
GAA c.2646+2T>A ( ENST00000302262.8, ENST00000390015.7, ENST00000570803.6, ENST00000577106.6, ENST00000714054.1, ENST00000714055.1, ENST00000714057.1, ENST00000714058.1, ENST00000714062.1 )
Associated Disease
Glycogen storage disease, type II
Source Database
ClinVar
Description
NM_000152.5(GAA):c.2646+2T>A AND Glycogen storage disease, type II
ClinVar Allele ID
187019
ClinVar RefSeq Alternation Syntax
NM_001079803.3:c.2646+2T>A
ClinVar RefSeq Alternation Syntax
NM_000152.5:c.2646+2T>A
ClinVar RefSeq Alternation Syntax
NM_001079804.3:c.2646+2T>A
ClinVar RefSeq Alternation Syntax
NM_001406741.1:c.2646+2T>A
ClinVar RefSeq Alternation Syntax
NM_001406742.1:c.2646+2T>A
Clinical Significance Description
Likely pathogenic
Clinical Significance Last Update
2020-04-20
Clinical Significance Review Status
reviewed by expert panel
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV000169291
ClinVar Disease
Glycogen storage disease, type II
Observed Origin Sample
germline
Observed Origin Sample
unknown
Drugs