Annotation Detail

Information
Associated Genes
ABCA4
Associated Variants
ABCA4 p.Arg1108Cys (p.R1108C) ( ENST00000370225.4 )
ABCA4 p.Arg1108Cys (p.R1108C) ( ENST00000370225.4 )
Associated Disease
Severe early-childhood-onset retinal dystrophy
Source Database
ClinVar
Description
NM_000350.3(ABCA4):c.3322C>T (p.Arg1108Cys) AND Severe early-childhood-onset retinal dystrophy
ClinVar Allele ID
98774
ClinVar RefSeq Alternation Syntax
NM_000350.3:c.3322C>T
ClinVar RefSeq Alternation Syntax
NM_001425324.1:c.3100C>T
Clinical Significance Description
Pathogenic/Likely pathogenic
Clinical Significance Last Update
2021-10-05
Clinical Significance Review Status
criteria provided, multiple submitters, no conflicts
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV000150052
ClinVar Disease
Severe early-childhood-onset retinal dystrophy
Observed Origin Sample
germline
Observed Origin Sample
unknown
Observed Origin Sample
maternal
Drugs