Annotation Detail

Information
Associated Genes
GNPTAB
Associated Variants
GNPTAB p.Leu785Trp (p.L785W) ( ENST00000299314.12 )
GNPTAB p.Leu785Trp (p.L785W) ( ENST00000299314.12 )
Associated Disease
Pseudo-Hurler polydystrophy
Source Database
ClinVar
Description
NM_024312.5(GNPTAB):c.2354T>G (p.Leu785Trp) AND Pseudo-Hurler polydystrophy
ClinVar Allele ID
106603
ClinVar RefSeq Alternation Syntax
NM_024312.5:c.2354T>G
Clinical Significance Description
Pathogenic
Clinical Significance Review Status
no assertion criteria provided
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV000087104
ClinVar Disease
Pseudo-Hurler polydystrophy
Observed Origin Sample
inherited
Drugs