Annotation Detail

Information
Associated Genes
IDUA
Associated Variants
IDUA p.Arg621Ter (p.R621*) ( ENST00000247933.9, ENST00000514224.2 )
IDUA p.Arg621Ter (p.R621*) ( ENST00000247933.9, ENST00000514224.2 )
Associated Disease
Hurler syndrome
Source Database
ClinVar
Description
NM_000203.5(IDUA):c.1861C>T (p.Arg621Ter) AND Hurler syndrome
ClinVar Allele ID
26956
ClinVar RefSeq Alternation Syntax
NR_110313.1:n.1953C>T
ClinVar RefSeq Alternation Syntax
NM_001363576.1:c.1465C>T
ClinVar RefSeq Alternation Syntax
NM_000203.5:c.1861C>T
Clinical Significance Description
Pathogenic
Clinical Significance Last Update
2017-06-30
Clinical Significance Review Status
criteria provided, single submitter
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV000012692
ClinVar Disease
Hurler syndrome
Observed Origin Sample
germline
Observed Origin Sample
unknown
Pubmed
7951228
Drugs