Annotation Detail

Information
Associated Genes
GNPTAB
Associated Variants
GNPTAB p.Asp407Ala (p.D407A) ( ENST00000299314.12, ENST00000549940.5 )
GNPTAB p.Asp407Ala (p.D407A) ( ENST00000299314.12, ENST00000549940.5 )
Associated Disease
Pseudo-Hurler polydystrophy
Source Database
ClinVar
Description
NM_024312.5(GNPTAB):c.1220A>C (p.Asp407Ala) AND Pseudo-Hurler polydystrophy
ClinVar Allele ID
17801
ClinVar RefSeq Alternation Syntax
NM_024312.5:c.1220A>C
Clinical Significance Description
Pathogenic
Clinical Significance Last Update
2012-05-10
Clinical Significance Review Status
no assertion criteria provided
URL
https://www.ncbi.nlm.nih.gov/clinvar/RCV000002889
ClinVar Disease
Pseudo-Hurler polydystrophy
Observed Origin Sample
germline
Observed Origin Sample
not provided
Pubmed
16094673
Drugs